Ceroid Storage Disease - 21 Studies Found
Recruiting |
: Clinical and Neuropsychological Investigations in Batten Disease : Neuronal Ceroid Lipofuscinosis : 2013-05-17 |
Terminated |
: Collection of Cerebrospinal Fluid in Healthy Children :
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Recruiting |
: Batten CLN6 Gene Therapy :
: 2016-03-16 : Drug: scAVV9.CB.CLN6 Six subjects with diagnosis of CLN6 disease will receive scAVV9.CB.CLN6 administere |
Completed |
: Genotype - Phenotype Correlations of LINCL :
: 2005-09-06 |
Active, not recruiting |
: A Multicenter, Multinational, Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease :
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Enrolling by invitation |
: A Safety, Tolerability, and Efficacy Study of Intracerebroventricular BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 Disease :
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Recruiting |
: Genetic Characterization of Movement Disorders and Dementias :
: 2015-04-03 |
Recruiting |
: UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells :
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Recruiting |
: Human Placental-Derived Stem Cell Transplantation :
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